Navigating the Niche – Forecasting in Ultra-Rare Diseases and Cell & Gene Therapies

Session details:

Forecasting for ultra-rare diseases and Cell & Gene Therapies (CGTs) defies traditional models. Despite minuscule patient populations, these high-stakes markets offer immense opportunity but demand new approaches due to data scarcity, complex logistics, and unique reimbursement models. This session provides commercial leaders and strategists practical insights to navigate these challenges. We’ll discuss innovative methodologies for patient identification, capacity-constrained launches, and value-based forecasting. Let us transform our forecast into a strategic compass, driving smarter decisions and ensuring life-changing innovations reach every patient.

Attendees will walk away from the session with:

·      An understanding of advanced methodologies for patient identification in ultra-rare diseases

·      A POV on developing capacity-constrained launch forecasts for CGTs, integrating logistics and infrastructure

·      A roadmap to utilize forecasting strategically to optimize market access, resource allocation, and portfolio decisions in niche markets